Click here to view – Newly released RARE 2030 Recommendations
These recommendations are intended for shaping a new policy framework for rare diseases over the next ten years to increase research and improve the care and quality of life of patients with rare diseases or rare cancers.
The UK and the Republic of Ireland run the only formal national programme for liver transplantation in patients with neuroendocrine tumours, and evidence shows those transplanted ...
Ongoing variability in the supply of pancreatic enzyme replacement therapy (PERT) — particularly Creon® 25,000iu capsules — has left some people struggling to obtain their prescription. ...